Glucocerebrosidase gene therapy - Sanofi
Alternative Names: Gaucher's disease gene therapy - SanofiLatest Information Update: 31 Mar 2022
At a glance
- Originator Nonindustrial source
- Developer Sanofi
- Class Gene therapies
- Mechanism of Action Gene transference; Glucosylceramidase replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Gaucher's disease
Most Recent Events
- 22 Jun 2005 Preclinical data presented at the 8th Annual Meeting of the American Society of Gene Therapy (ASGT-2005) have been added to the Metabolic disorders pharmacodynamics section
- 29 Jul 2003 Genzyme General, Genzyme Biosurgery and Genzyme Molecular Oncology are now called Genzyme Corporation
- 25 Jun 2003 Preclinical trials in Gaucher's disease in USA (IV-infusion)