Alpha-galactosidase gene therapy - Sanofi
Alternative Names: Fabry's disease gene therapy1Latest Information Update: 31 Mar 2022
At a glance
- Originator Genzyme Corporation
- Developer Sanofi
- Class Gene therapies
- Mechanism of Action Alpha-galactosidase stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Fabry's disease
Most Recent Events
- 04 May 2006 No development reported - Preclinical for Fabry's disease in USA (unspecified route)
- 29 Jul 2003 Genzyme General, Genzyme Biosurgery and Genzyme Molecular Oncology are now called Genzyme Corporation
- 09 Aug 2002 This gene therapy is still in active development