Factor VIII gene therapy - Targeted Genetics
Latest Information Update: 24 Oct 2021
Price :
$50 *
At a glance
- Originator University of North Carolina
- Class Blood coagulation factors; Coagulants
- Mechanism of Action Blood coagulation factor replacements; Factor X stimulants; Gene transference
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Haemophilia A