Research programme: familial hypercholesterolaemia gene therapy - Amsterdam Molecular Therapeutics
Alternative Names: Familial hypercholesterolaemia gene therapy research programme - AMT; LDL-R gene therapy; Research programme: familial hypercholesterolaemia gene therapy - AMTLatest Information Update: 08 Sep 2006
At a glance
- Originator Amsterdam Molecular Therapeutics
- Class
- Mechanism of Action LDL receptor agonists
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
Highest Development Phases
- Discontinued Hyperlipoproteinaemia type II
Most Recent Events
- 08 Sep 2006 Discontinued - Preclinical for Familial hypercholesterolaemia in Netherlands (unspecified route)
- 20 Jul 2004 This programme is still in active development - BIO 2004 Annual International Convention (BIO-2004)
- 29 Mar 2001 Preclinical development for Familial hypercholesterolaemia in Netherlands (Unknown route)