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RPE65 gene therapy

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Drug Profile

RPE65 gene therapy

Alternative Names: REP 65 gene therapy

Latest Information Update: 24 Oct 2021

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At a glance

  • Originator Nonindustrial source
  • Class
  • Mechanism of Action
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No

Highest Development Phases

  • No development reported Blindness

Most Recent Events

  • 07 May 2001 Preclinical development for Leber congenital amaurosis in USA (Intraocular)

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