Drug Profile
Pegvaliase - BioMarin Pharmaceutical
Alternative Names: BMN-165; Palynziq; PEG-PAL; Pegvaliase-pqpz; PEGylated phenylalanine ammonia lyase; Pegylated recombinant Anabaena variabilis phenylalanine ammonia lyase; PEGylated recombinant phenylalanine ammonia lyase; Phenylase; rAvPAL-PEGLatest Information Update: 05 Nov 2023
Price :
$50
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At a glance
- Originator IBEX Technologies
- Developer BioMarin Pharmaceutical
- Class Ammonia lyases; Enzymes; Recombinant proteins
- Mechanism of Action Phenylalanine ammonia lyase replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Marketed Phenylketonuria