SCID-X1 gene therapy - AVAX
Alternative Names: SCID gene therapy - AVAX; SCID-XI gene therapyLatest Information Update: 06 Feb 2017
At a glance
- Originator Necker Hospital
- Developer AVAX Technologies; Necker Hospital
- Class Gene therapies
- Mechanism of Action Lymphocyte stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Severe combined immunodeficiency
Most Recent Events
- 06 Feb 2017 Discontinued - Phase-I/II for Severe Combined Immunodeficiency in France (unspecified route)
- 24 Jan 2005 Suspended - Phase I/II for Severe Combined Immunodeficiency in France (unspecified route)
- 24 May 2004 Phase I/II trials in Severe Combined Immunodeficiency in France (unspecified route)