Drug Profile
Trofinetide - ACADIA Pharmaceuticals/Neuren Pharmaceuticals
Alternative Names: DAYBUE; G-2Me-PE; Glycyl-2-methyl-L-prolyl-L-glutamic acid; Glycyl-L-2-methylprolyl-L-glutamic acid; NNZ-2566Latest Information Update: 07 Feb 2024
Price :
$50
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At a glance
- Originator Neuren Pharmaceuticals
- Developer ACADIA Pharmaceuticals; Neuren Pharmaceuticals; Walter Reed Army Institute of Research
- Class Anti-inflammatories; Glutamates; Neuropeptides; Neuroprotectants; Oligopeptides; Pyrrolidines; Small molecules
- Mechanism of Action Astrocyte inhibitors; Cytokine inhibitors; Glial cell inhibitors; Insulin-like growth factor I stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Marketed Rett syndrome
- Phase II Brain injuries; Fragile X syndrome; Traumatic brain injuries
- Discontinued Autistic disorder; Multiple sclerosis
Most Recent Events
- 31 Jan 2024 Acadia Pharmaceuticals plans a New Drug Submission (NDS) for Trofinetide in Canada in Q1 2024
- 31 Jan 2024 Neuren Pharmaceuticals announces intention to engage with Japanese PMDA for Rett syndrome in 2024
- 31 Jan 2024 Neuren Pharmaceuticals announces intention to submit MAA to EMA for Rett syndrome in H1 2025