Drug Profile
NNZ 2591
Alternative Names: ACP-2591; Cyclo-L-Glycyl-L-2-Allylproline; NNZ-2591Latest Information Update: 07 Feb 2024
Price :
$50
*
At a glance
- Originator Neuren Pharmaceuticals
- Developer ACADIA Pharmaceuticals; Neuren Pharmaceuticals
- Class 2 ring heterocyclic compounds; Alkenes; Antiparkinsonians; Behavioural disorder therapies; Cyclic peptides; Neuroprotectants; Nootropics; Piperazines; Pyrazines; Pyrroles; Small molecules; Vascular disorder therapies
- Mechanism of Action Cell death inhibitors; Neuropeptide receptor modulators; Symporter modulators; Synaptic transmission modulators
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase II Angelman syndrome; Pitt-Hopkins syndrome; Prader-Willi syndrome; Telomeric 22q13 Monosomy Syndrome
- Phase I Fragile X syndrome; Rett syndrome
Most Recent Events
- 31 Jan 2024 Neuren Pharmaceuticals completes enrolment in its phase-II trial for Angelman syndrome (In children, In adolescents) in Australia (PO), (NCT05011851)
- 31 Jan 2024 Neuren Pharmaceuticals plans phase-III trials for multiple indications
- 18 Dec 2023 Efficacy and safety data from a phase II clinical trials in Telomeric 22q13 Monosomy Syndrome released by Neuren Pharmaceuticals