Research programme: alpha-1 antitrypsin deficiency gene therapy - VIRxSYS
Latest Information Update: 04 Nov 2017
At a glance
- Originator Intronn
- Developer VIRxSYS Corporation
- Class Gene therapies
- Mechanism of Action Trypsin inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
Highest Development Phases
- No development reported Alpha 1-antitrypsin deficiency
Most Recent Events
- 04 Nov 2017 No recent reports of development identified for preclinical development in Alpha-1-antitrypsin-deficiency in USA (Parenteral)
- 18 Nov 2011 Preclinical trials in Alpha 1-antitrypsin deficiency in USA (Parenteral)
- 21 Sep 2007 This programme is still in active development