Research programme: Huntington's disease therapeutics - CHDI/Ionis Pharmaceuticals/KineMed
Alternative Names: ISIS 387898; ISIS 388241; ISIS 408737Latest Information Update: 04 Nov 2017
At a glance
- Originator Isis Pharmaceuticals
- Developer Ionis Pharmaceuticals
- Class Antisense oligonucleotides
- Mechanism of Action Protein synthesis inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Huntington's disease