Research programme: amyotrophic lateral sclerosis therapy - Targeted Genetics
Latest Information Update: 11 Nov 2010
At a glance
- Originator Targeted Genetics Corporation; University of Iowa
- Class Small molecules
- Mechanism of Action
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
Highest Development Phases
- Discontinued Amyotrophic lateral sclerosis
Most Recent Events
- 31 Mar 2009 Preclinical trials in Amyotrophic lateral sclerosis in USA (unspecified route)