Elivaldogene tavalentivec - bluebird bio

Drug Profile

Elivaldogene tavalentivec - bluebird bio

Alternative Names: Adrenoleucodystrophy gene therapy - bluebird bio; Lenti-D

Latest Information Update: 07 Aug 2018

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At a glance

  • Originator Genetix Pharmaceuticals; INSERM
  • Developer bluebird bio
  • Class Adrenoleucodystrophy gene therapies; Gene therapies
  • Mechanism of Action ALDP expression stimulants; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Adrenoleucodystrophy
  • New Molecular Entity No

Highest Development Phases

  • Phase II/III Adrenoleucodystrophy

Most Recent Events

  • 31 Jul 2018 Elivaldogene tavalentivec receives Priority Medicine (PRIME) status for Adrenoleucodystrophy in European Union
  • 25 May 2018 Elivaldogene tavalentivec - bluebird bio receives Breakthrough Therapy status for Adrenoleucodystrophy (In children) in USA
  • 25 May 2018 Lenti-D™ receives rare paediatric disease designation for Adrenoleukodystrophy in the US
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