Drug Profile
BMN 044
Alternative Names: BMN044; Exon 44 specific phosphorothioate oligonucleotide; H44aon188; PRO044; PS 188Latest Information Update: 02 Oct 2021
Price :
$50
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At a glance
- Originator Prosensa
- Developer BioMarin Nederland
- Class Antisense oligonucleotides
- Mechanism of Action Antisense RNA modulators; Dystrophin stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Duchenne muscular dystrophy