Research programme: antisense drug therapies - GlaxoSmithKline/Ionis Pharmaceuticals/ProQR Therapeutics
Alternative Names: ISIS GSK6 LRx; ISIS-AATRxLatest Information Update: 28 Dec 2017
At a glance
- Originator Isis Pharmaceuticals
- Developer Ionis Pharmaceuticals; Isis Pharmaceuticals
- Class Antisense oligonucleotides; Eye disorder therapies
- Mechanism of Action Alpha 1 adrenergic receptor modulators; Alpha 1-antitrypsin modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Alpha 1-antitrypsin deficiency; Blindness; Eye disorders; Infections
Most Recent Events
- 28 Dec 2017 No recent reports of development identified for preclinical development in Eye-disorders in USA
- 04 Nov 2017 No recent reports of development identified for preclinical development in Blindness in USA
- 04 Nov 2017 No recent reports of development identified for preclinical development in Infections in USA