Drug Profile
Research programme: apolipoprotein B100 gene therapy - uniQure
Alternative Names: ApoB100 gene therapy - uniQureLatest Information Update: 16 Jul 2012
Price :
$50
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At a glance
- Originator Amsterdam Molecular Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
Highest Development Phases
- Discontinued Hypercholesterolaemia