Research programme: microRNA therapeutics - Novartis/Sanofi
Alternative Names: anti-miR-21; microRNA-21 therapeutics; microRNA-221/microRNA-222 therapeutics; miR-221/222 therapeutics; miRNA-21 therapeuticsLatest Information Update: 01 Jul 2025
At a glance
- Originator Regulus Therapeutics; sanofi-aventis
- Developer Novartis; Sanofi
- Class MicroRNAs; Oligonucleotides
- Mechanism of Action RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Nephritis
- No development reported Fibrosis; Liver cancer
Most Recent Events
- 25 Jun 2025 Regulus Therapeutics has been acquired and merged into Novartis
- 16 Jul 2016 No recent reports of development identified for preclinical development in Fibrosis in USA
- 16 Jul 2016 No recent reports of development identified for preclinical development in liver cancer in USA