GSK 2696273
Alternative Names: 2696273; Adenosine deaminase severe combined immune deficiency therapy - GlaxoSmithKline; GSK-2696273; StrimvelisLatest Information Update: 02 Feb 2024
Price :
$50 *
At a glance
- Originator The San Raffaele Telethon Institute for Gene Therapy
- Developer Orchard Therapeutics
- Class Gene therapies; Haematopoietic stem cells therapies; Stem cell therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Marketed Adenosine deaminase deficiency