Drug Profile
Cyclic pyranopterin monophosphate - Origin Biosciences
Alternative Names: ALXN-1101; BBP-870; cPMP; cPMP-cpd; ORGN001Latest Information Update: 05 Dec 2019
Price :
$50
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At a glance
- Originator Orphatec Pharmaceuticals
- Developer Origin Biosciences
- Class Organophosphorus compounds; Pterins
- Mechanism of Action Molybdenum cofactor replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Preregistration Molybdenum cofactor deficiency