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Fosdenopterin - Origin Biosciences

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Drug Profile

Fosdenopterin - Origin Biosciences

Alternative Names: ALXN-1101; BBP-870; cPMP; cPMP-cpd; Cyclic pyranopterin monophosphate (cPMP) replacement therapy - Origin Biosciences; Cyclic pyranopterin monophosphate - Origin Biosciences; Nulibry; ORGN 001

Latest Information Update: 23 Apr 2024

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At a glance

  • Originator Orphatec Pharmaceuticals
  • Developer BridgeBio Pharma; Origin Biosciences; Sentynl Therapeutics
  • Class Alkadienes; Amines; Aza compounds; Ketones; Organophosphorus compounds; Pterins; Pyrans; Small molecules
  • Mechanism of Action Molybdenum cofactor replacements
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Molybdenum cofactor deficiency
  • New Molecular Entity Yes

Highest Development Phases

  • Marketed Molybdenum cofactor deficiency

Most Recent Events

  • 16 Apr 2024 Registered for Molybdenum cofactor deficiency (In children, In infants, In neonates) in United Kingdom (IV)
  • 16 Apr 2024 BridgeBio Pharma intends to file NDA to Medicine and Healthcare products Regulatory Agency for Molybdenum cofactor deficiency (MoCD) Type A in the UK in the coming months
  • 17 Oct 2022 Origin Biosciences completes a phase II/III trial in in Molybdenum cofactor deficiency (In children, In infants, In neonates) in the US, Israel, Norway, Spain, Turkey and the United Kingdom (NCT02629393) (EudraCT2013-002702-30)

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