Hereditary inclusion body myopathy gene therapy - Gradalis
Alternative Names: GNE LipoplexLatest Information Update: 16 Jul 2016
At a glance
- Originator Gradalis
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Nonaka distal myopathy
Most Recent Events
- 16 Jul 2016 No recent reports of development identified for phase-I development in Nonaka distal myopathy in USA (Parenteral)