Research programme: haemophilia therapeutics - Ascension Healthcare/PolyTherics
Alternative Names: ChapAte; Haemophilia therapeutics - Ascension Healthcare; Haemophilia therapeutics - Celtic Pharma/PolyTherics; Long-acting blood coagulation factor IX - Ascension Healthcare; Long-acting blood coagulation factor VIIa -Ascension Healthcare; Long-acting blood coagulation factor VIII -Ascension Healthcare; PBB 8 CH; PBB 8 SQ; Protein therapeutics - Celtic Pharma/Polytherics; SubcutAte; TheraPEG™ Factor IX; TheraPEG™ Factor VIIa; TheraPEG™ Factor VIIILatest Information Update: 28 Jan 2021
At a glance
- Originator Celtic Pharma; PolyTherics
- Developer Ascension Healthcare; PolyTherics
- Class Blood coagulation factors; Polyethylene glycols
- Mechanism of Action Blood coagulation factor replacements; Factor IX stimulants; Factor VIII replacements; Factor X stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Haemophilia A; Haemophilia B
Most Recent Events
- 28 Jan 2021 No recent reports of development identified for preclinical development in Haemophilia-A in United Kingdom (SC, Injection)
- 23 Jan 2019 Preclinical development is ongoing in United Kingdom (SC, Injection) (Ascension Healthcare pipeline, January 2019)
- 04 Jan 2019 Ascension Healthcare plans a phase II trials of SubcutAte and ChapAte programmes for Haemophilia A in 2019 (Ascension Healthcare pipeline, January 2019)