Research programme: CFTR modulators - Cystic Fibrosis Foundation Therapeutics/Sanofi
Alternative Names: CFTR correctors - Cystic Fibrosis Foundation Therapeutics/SanofiLatest Information Update: 31 Mar 2022
At a glance
- Originator Cystic Fibrosis Foundation Therapeutics; Genzyme Corporation
- Developer Cystic Fibrosis Foundation Therapeutics; Sanofi
- Class
- Mechanism of Action ATP-binding cassette transporter modulators; Cystic fibrosis transmembrane conductance regulator modulators
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Cystic fibrosis
Most Recent Events
- 16 Jul 2016 No recent reports of development identified for research development in Cystic-fibrosis in USA
- 16 Nov 2011 Early research in Cystic fibrosis in USA (unspecified route)