Drug Profile
Research programme: sarcoplasmic reticulum calcium-transporting ATPase stimulants - PTC Therapeutics
Alternative Names: DBMD-SERCA2aLatest Information Update: 16 Jul 2016
Price :
$50
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At a glance
- Originator PTC Therapeutics
- Class Small molecules
- Mechanism of Action Sarcoplasmic reticulum calcium-transporting ATPase stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
Highest Development Phases
- No development reported Duchenne muscular dystrophy
Most Recent Events
- 16 Jul 2016 No recent reports of development identified for research development in Duchenne muscular dystrophy in USA
- 01 Feb 2011 Early research in Duchenne muscular dystrophy in USA (unspecified route)