Patisiran - Alnylam Pharmaceuticals

Drug Profile

Patisiran - Alnylam Pharmaceuticals

Alternative Names: ALN-TTR02; GENZ-438027; SAR-438037

Latest Information Update: 04 May 2018

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At a glance

  • Originator Alnylam Pharmaceuticals
  • Class Oligonucleotides; Small interfering RNA
  • Mechanism of Action RNA interference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Amyloid polyneuropathy
  • New Molecular Entity Yes

Highest Development Phases

  • Preregistration Amyloidosis
  • Phase III Amyloid polyneuropathy

Most Recent Events

  • 21 Apr 2018 Efficacy and safety data from phase III APOLLO trial presented at the 70th Annual Meeting of the American Academy of Neurology (AAN-2018)
  • 28 Mar 2018 Efficacy and adverse events data from a cardiac sub-population of the phase III APOLLO trial in Amyloid polyneuropathy released by Alnylam
  • 28 Mar 2018 Efficacy and adverse events data from the phase III APOLLO-OLE trial in Amyloid polyneuropathy released by Alnylam
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