Vamorolone - Santhera Pharmaceuticals
Alternative Names: AGAMREE; VB-15; VBP-15Latest Information Update: 06 May 2024
At a glance
- Originator ReveraGen BioPharma
- Developer ReveraGen BioPharma; Santhera Pharmaceuticals; Sperogenix Therapeutics
- Class Anti-inflammatories; Antianaemics; Antiasthmatics; Antifibrotics; Antineoplastics; Antirheumatics; Corticosteroids; Glucocorticoids; Pregnatrienes; Small molecules
- Mechanism of Action Glucocorticoid receptor agonists; Mineralocorticoid receptor antagonists
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Marketed Duchenne muscular dystrophy
- Preclinical Unspecified
- Discontinued Amyotrophic lateral sclerosis; Asthma; Brain cancer; Cystic fibrosis; Inflammatory bowel diseases; Multiple sclerosis; Rheumatoid arthritis; Sickle cell anaemia; Spinal muscular atrophy
Most Recent Events
- 06 May 2024 Santhera Pharmaceuticals initiates a early access programme for Duchenne muscular dystrophy in France
- 25 Apr 2024 Santhera Pharmaceuticals anticipates approval of vamorolone for Duchenne muscular dystrophy in China in Q1 2025
- 25 Apr 2024 Santhera Pharmaceuticals announces intention to launch vamorolone for the treatment of Duchenne muscular dystrophy (In children, In adolescents, In adults, In the elderly) in the United Kingdom in 2024