Deramiocel - Capricor Therapeutics
Alternative Names: Allogeneic adult stem cell therapy for myocardial infarction - Capricor; Allogeneic cardiosphere-derived cells - Capricor; Allogeneic CDCs - Capricor; Allogenic derived cells - Capricor; CAP-1002Latest Information Update: 25 Jun 2025
At a glance
- Originator Capricor
- Developer Capricor; Capricor Therapeutics; Medical University of South Carolina
- Class Exosome therapies; Stem cell therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
- Available For Licensing Yes
Highest Development Phases
- Preregistration Duchenne muscular dystrophy
- Phase II COVID 2019 infections
- Phase I/II Cardiomyopathies
- Discontinued Heart failure; Myocardial infarction
Most Recent Events
- 20 Jun 2025 Efficacy and adverse events data from the phase II open label extension of the HOPE-2 trial in Duchenne Muscular Dystrophy released by Capricor Therapeutics
- 17 Jun 2025 Capricor Therapeutics plans a commercial launch of deramiocel for Duchenne muscular dystrophy
- 13 Jun 2025 Deramiocel - Capricor Therapeutics receives Orphan Drug status for Becker muscular dystrophy in USA