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Research programme: gene editing therapeutics - Intellia Therapeutics/Regeneron Pharmaceuticals

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Drug Profile

Research programme: gene editing therapeutics - Intellia Therapeutics/Regeneron Pharmaceuticals

Alternative Names: CRISPR/Cas9 gene editing therapies - Intellia Therapeutics/Regeneron Pharmaceuticals

Latest Information Update: 28 Jul 2024

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At a glance

  • Originator Intellia Therapeutics
  • Developer Intellia Therapeutics; Regeneron Pharmaceuticals
  • Class Antihaemorrhagics; Blood coagulation factors; Coagulants; Gene therapies
  • Mechanism of Action Factor VIII modulators; Gene modulators; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Research Musculoskeletal disorders; Neurological disorders
  • No development reported Haemophilia A; Transthyretin-related hereditary amyloidosis

Most Recent Events

  • 28 Jul 2024 No recent reports of development identified for research development in Haemophilia-A in USA (Parenteral)
  • 31 Mar 2024 Intellia Therapeutics opt-out rights for gene editing therapeutics
  • 02 Nov 2023 Regeneron and Intellia Therapeutics expands existing collaboration to develop products for the treatment of Neurological and Muscular disorders

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