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Research programme: inborn metabolic disorder therapeutics - Agios Pharmaceuticals

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Drug Profile

Research programme: inborn metabolic disorder therapeutics - Agios Pharmaceuticals

Alternative Names: IEM therapeutics - Agios Pharmaceuticals

Latest Information Update: 28 Jun 2022

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At a glance

  • Originator Agios Pharmaceuticals
  • Class Small molecules
  • Mechanism of Action Glycolysis modulators; Pyruvate kinase stimulants; Thyroid hormone binding protein stimulants
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity Yes

Highest Development Phases

  • No development reported Beta-thalassaemia; Friedreich's ataxia; Inborn genetic disorders

Most Recent Events

  • 28 Jun 2022 No recent reports of development identified for research development in Friedreich's ataxia in USA
  • 28 Mar 2022 No recent reports of development identified for preclinical development in Inborn genetic disorders in USA
  • 28 Dec 2020 No recent reports of development identified for research development in Beta-thalassaemia in USA

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