Research programme: inborn metabolic disorder therapeutics - Agios Pharmaceuticals
Alternative Names: IEM therapeutics - Agios PharmaceuticalsLatest Information Update: 28 Jun 2022
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At a glance
- Originator Agios Pharmaceuticals
- Class Small molecules
- Mechanism of Action Glycolysis modulators; Pyruvate kinase stimulants; Thyroid hormone binding protein stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Beta-thalassaemia; Friedreich's ataxia; Inborn genetic disorders
Most Recent Events
- 28 Jun 2022 No recent reports of development identified for research development in Friedreich's ataxia in USA
- 28 Mar 2022 No recent reports of development identified for preclinical development in Inborn genetic disorders in USA
- 28 Dec 2020 No recent reports of development identified for research development in Beta-thalassaemia in USA