Research programme: RNA-based therapeutics - ethris/Takeda
Latest Information Update: 21 Mar 2023
At a glance
- Originator ethris; Shire
- Developer ethris; Takeda
- Class RNA
- Mechanism of Action Bone morphogenetic protein receptor type II modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Bone disorders; Cystic fibrosis; Lung disorders
Most Recent Events
- 21 Mar 2023 Discontinued - Preclinical for Bone disorders in Germany (Implant)
- 21 Mar 2023 Discontinued - Preclinical for Cystic fibrosis in Germany (IM)
- 21 Mar 2023 Discontinued - Preclinical for Lung disorders in Germany (IM)