Lucerastat - Idorsia Pharmaceuticals

Drug Profile

Lucerastat - Idorsia Pharmaceuticals

Alternative Names: ACT-434964; OGT-923

Latest Information Update: 28 Mar 2018

Price : *
* Final gross price and currency may vary according to local VAT and billing address.
* Your purchase entitles you to full access to the information contained in our drug profile at the time of purchase. A link to download a PDF version of the drug profile will be included in your email receipt. Adis is an information provider. We do not sell or distribute the pharmaceutical compounds written about in this database.

At a glance

  • Originator Actelion Pharmaceuticals
  • Developer Actelion Pharmaceuticals; Idorsia Pharmaceuticals
  • Class Antihyperlipidaemics; Piperidines; Small molecules
  • Mechanism of Action Glucosylceramide synthase inhibitors
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Fabry's disease
  • New Molecular Entity Yes

Highest Development Phases

  • No development reported Fabry's disease; Lipid metabolism disorders

Most Recent Events

  • 28 Mar 2018 No recent reports of development identified for phase-I development in Fabry's-disease in Germany (PO, Capsule)
  • 06 Feb 2018 Actelion plans a pivotal phase III trial for Fabry's disease in the first half of 2018 (NCT03425539)
  • 06 Feb 2018 Lucerastat receives Orphan Drug status for Fabry's disease in European Union before February 2018
Restricted Access

Oops, it looks like you don’t have a valid subscription to this content. To gain full access to the content and functionality of the AdisInsight database try one of the following.

  • with a username/password associated to an account with a valid subscription
  • Contact your organization’s admin about adding this content to your AdisInsight subscription
  • Request a trial

If you are a subscriber to this content then contact us at so we can help.

Back to top