Research programme: RNA interference-based technology - Alnylam
Alternative Names: KC2; MC3; MC3 LNP; MD1; reLNPLatest Information Update: 11 Nov 2021
At a glance
- Originator Alnylam Pharmaceuticals
- Developer AlCana Technologies; Alnylam Pharmaceuticals; Icahn School of Medicine at Mount Sinai; Massachusetts General Hospital; Massachusetts Institute of Technology; University of Bonn; University of British Columbia
- Class Small interfering RNA
- Mechanism of Action CCR2 receptor antagonists; Claudin 3 inhibitors; DNA-directed RNA polymerase inhibitors; RNA interference; TOR1A protein inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
Highest Development Phases
- No development reported Autoimmune disorders; Cancer; Dystonia; Inflammation; Influenza A virus infections
Most Recent Events
- 17 Jan 2013 No development reported - Preclinical for Cancer in Germany (Parenteral)
- 16 Jan 2013 Preclinical trials in Autoimmune disorders in USA (Parenteral)
- 12 Nov 2012 Alnylam Pharmaceuticals and Tekmira Pharmaceuticals Corporation sign a new licensing agreement regarding RNAi-based therapies, superseding all previous agreements, and resolve all litigation