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Research programme: rare disease mRNA therapeutics - Moderna Therapeutics

Drug Profile

Research programme: rare disease mRNA therapeutics - Moderna Therapeutics

Alternative Names: Antibody messenger RNA therapeutics™; mRNA-3630; MT-004; MT-026; MT-033; MT-039; MT-059; MT-088; MT-104

Latest Information Update: 12 May 2020

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At a glance

  • Originator Moderna Therapeutics
  • Class Antihaemorrhagics; RNA
  • Mechanism of Action Alpha-galactosidase stimulants; Protein synthesis stimulants
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Propionic acidaemia
  • New Molecular Entity Yes
  • Available For Licensing Yes

Highest Development Phases

  • No development reported Haemophilia
  • Discontinued Fabry's disease

Most Recent Events

  • 07 May 2020 Discontinued - Preclinical for Fabry's disease in USA (Parenteral)
  • 05 Feb 2019 Moderna Therapeutics plans to file an IND application for mRNA 3630 for Fabry disease
  • 05 Feb 2019 Moderna Therapeutics plans a clinical trial for Fabry disease for mRNA 3630
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