PDA 002
Alternative Names: PDA-002; PDAC cells; Placental-derived adherent cells intramuscularLatest Information Update: 16 Oct 2024
At a glance
- Originator Celgene Corporation
- Developer Celgene Corporation; Celularity
- Class Skin disorder therapies; Stem cell therapies; Vascular disorder therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Facioscapulohumeral muscular dystrophy
- Discontinued Diabetic foot ulcer; Diabetic neuropathies; Peripheral arterial disorders
Most Recent Events
- 15 Oct 2024 Phase-I/II clinical trials in Facioscapulohumeral muscular dystrophy in USA (Parenteral), (Celularity pipeline, October 2024)
- 20 Mar 2024 Celularity plans a phase I/II trial for Facioscapulohumeral Muscular Dystrophy in the second half of 2024
- 20 Mar 2024 Celularity submits Orphan Drug designation application to US FDA for Facioscapulohumeral Muscular Dystrophy