Drug Profile
VX 983
Alternative Names: VX-983Latest Information Update: 12 Nov 2020
Price :
$50
*
At a glance
- Originator Cystic Fibrosis Foundation Therapeutics; Vertex Pharmaceuticals
- Developer Vertex Pharmaceuticals
- Class Small molecules
- Mechanism of Action Cystic fibrosis transmembrane conductance regulator stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Cystic fibrosis