Drug Profile
Research programme: lysosomal storage disease enzyme replacement therapies - Angiochem
Alternative Names: MPS I Enzyme-Peptide conjugates - Angiochem; Mucopolysaccharidosis I Enzyme-Peptide conjugates - AngiochemLatest Information Update: 28 Oct 2020
Price :
$50
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At a glance
- Originator AngioChem
- Class Enzymes; Recombinant fusion proteins
- Mechanism of Action Iduronate sulfatase replacements; Iduronidase replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Mucopolysaccharidosis I; Mucopolysaccharidosis II
Most Recent Events
- 28 Oct 2020 No recent reports of development identified for research development in Mucopolysaccharidosis-II in Canada (Parenteral)
- 28 Feb 2018 No recent reports of development identified for research development in Mucopolysaccharidosis-I in Canada (Parenteral)
- 08 Sep 2016 Early research in Mucopolysaccharidosis II in Canada (Parenteral) before September 2016 (Angiochem Pipeline, September 2016)