Cholic acid - Asklepion
Alternative Names: Cholbam; Cholic acid FGK; KolbamLatest Information Update: 07 Jan 2025
At a glance
- Originator Asklepion Pharmaceuticals
- Developer Asklepion Pharmaceuticals; FGK Representative Service; Travere Therapeutics
- Class Choleretics; Cholic acids; Gallstone therapies; Small molecules
- Mechanism of Action Cholesterol 7 alpha hydroxylase inhibitors; Farnesoid X-activated receptor modulators; Sodium-bile acid cotransporter modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Marketed Inborn genetic disorders; Infantile Refsum disease; Peroxisomal disorders; Zellweger syndrome
Most Recent Events
- 07 Jan 2025 Discontinued - Phase-III for Inborn genetic disorders in Asia (PO)
- 07 Jan 2025 Discontinued - Phase-III for Inborn genetic disorders in Canada (PO)
- 07 Jan 2025 Discontinued - Phase-III for Inborn genetic disorders in South America (PO)