Drug Profile
Research programme: AAV-based gene therapies - 4D Molecular Therapeutics/Roche
Latest Information Update: 11 May 2015
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At a glance
- Originator Roche
- Developer 4D Molecular Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Unspecified