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Pariglasgene brecaparvovec - Dimension Therapeutics

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Drug Profile

Pariglasgene brecaparvovec - Dimension Therapeutics

Alternative Names: AAV gene therapy - Dimension; AAV8G6PC; Adeno-associated virus vector gene therapy - Dimension; DTX-401

Latest Information Update: 11 Mar 2026

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At a glance

  • Originator Dimension Therapeutics
  • Developer Dimension Therapeutics; Ultragenyx Pharmaceutical
  • Class Gene therapies
  • Mechanism of Action Gene transference; Glucose-6-phosphatase replacements
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Glycogen storage disease type I
  • New Molecular Entity No

Highest Development Phases

  • Preregistration Glycogen storage disease type I

Most Recent Events

  • 23 Feb 2026 Pariglasgene brecaparvovec receives Rare Pediatric Disease designation for Glycogen storage disease type I in USA
  • 23 Feb 2026 FDA assigns PDUFA action date of 23/08/2026 for pariglasgene brecaparvovec for Glycogen storage disease type I (IV, Infusion)
  • 23 Feb 2026 Glycogen storage disease type I receives priority review status for Glycogen storage disease type I in USA

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