Mavacamten - Bristol Myers Squibb
Alternative Names: BMS-986427; Camzaios; CAMZYOS; Camzyos; HCM 1; MAVA-Bristol Myers Squibb/Myokardia; MYK 461; SAR-439152Latest Information Update: 09 Apr 2026
At a glance
- Originator MyoKardia
- Developer Bristol-Myers Squibb; LianBio; MyoKardia
- Class Cardiovascular therapies; Ethylamines; Heart failure therapies; Pyrimidinones; Small molecules
- Mechanism of Action Cardiac myosin inhibitors
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Orphan Drug Status
Yes - Hypertrophic cardiomyopathy
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Marketed Hypertrophic cardiomyopathy
- Phase II Heart failure
Most Recent Events
- 29 Mar 2026 Updated efficacy and adverse events data from a phase III trial in Hypertrophic cardiomyopathy released by Bristol Myers Squibb
- 16 Jan 2026 MyoKardia completes phase-II/III MAVA-LTE trial Hypertrophic cardiomyopathy in USA, Belgium, Czech Republic, Denmark, France, Germany, Israel, Italy, Netherlands, Poland, Portugal, Spain and United Kingdom (PO) (NCT03723655)
- 12 Jan 2026 Efficacy and adverse events data from a phase III trial in Hypertrophic cardiomyopathy released by Bristol Myers Squibb