Research programme: genome editing therapeutics - Editas Medicine
Alternative Names: LCA10 programLatest Information Update: 15 May 2024
At a glance
- Originator Editas Medicine
- Class Antiulcers; Antivirals; Eye disorder therapies; Gene therapies
- Mechanism of Action Gene modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Retinitis pigmentosa
- No development reported Alpha 1-antitrypsin deficiency; Cystic fibrosis; Duchenne muscular dystrophy; Eye disorders; Herpes simplex virus type 1 infections; Leber congenital amaurosis; Usher syndromes
Most Recent Events
- 08 May 2024 Editas Medicine initiates appeal of the Patent Trial and Appeal Board decision favouring Broad Institute for CRISPR patent interference in the USA
- 28 Sep 2023 No recent reports of development identified for preclinical development in Usher-syndromes in USA (Ophthalmic, Injection)
- 28 Feb 2022 The US Patent and Trademark Office issues decision in favor of Broad Institute for interference claim for patent related to CRISPR-Cas9 genome editing technology in USA