Drug Profile
Research programme: orphan disease therapeutics - Aevi Genomic Medicine/The Childrens Hospital of Philadelphia
Alternative Names: AEVI-005; MDGN-204; MDGN-206Latest Information Update: 13 Mar 2018
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At a glance
- Originator Medgenics; The Childrens Hospital of Philadelphia
- Developer Aevi Genomic Medicine; Kyowa Hakko Kirin; The Childrens Hospital of Philadelphia
- Class Gene therapies; Monoclonal antibodies
- Mechanism of Action Immunomodulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Metabolic disorders
- Research Autoimmune disorders