Research programme: topoisomerase inhibitors - University of North Carolina School of Medicine/Unknown company
Alternative Names: Paternal UBE3A gene expression stimulant; UBE3A protein stimulantsLatest Information Update: 04 Nov 2017
At a glance
- Originator Unknown
- Developer University of North Carolina at Chapel Hill School of Medicine; Unknown
- Class
- Mechanism of Action DNA topoisomerase inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Angelman syndrome
Most Recent Events
- 04 Nov 2017 No recent reports of development identified for research development in Angelman-syndrome in USA
- 01 Oct 2013 Early research in Angelman syndrome in USA (unspecified route)