Research programme: eye disorder gene therapies - Beacon Therapeutics/4D Molecular Therapeutics
Latest Information Update: 29 Jun 2023
At a glance
- Originator Applied Genetic Technologies Corporation
- Developer Beacon Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Eye disorders
Most Recent Events
- 28 May 2019 No recent reports of development identified for preclinical development in Eye-disorders in USA (Parenteral)
- 20 Apr 2015 Applied Genetic Technologies Corporation in-licenses AAV vector discovery and optimization technology from 4D Molecular Therapeutics
- 20 Apr 2015 Preclinical trials in Eye disorders in USA (Parenteral)