BLU 554

Drug Profile

BLU 554

Alternative Names: BLU-554

Latest Information Update: 12 Sep 2017

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At a glance

  • Originator Blueprint Medicines
  • Class Antineoplastics; Small molecules
  • Mechanism of Action Type 4 fibroblast growth factor receptor antagonists
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Hepatocellular carcinoma
  • New Molecular Entity Yes

Highest Development Phases

  • Phase I Cholangiocarcinoma; Hepatocellular carcinoma

Most Recent Events

  • 21 Aug 2017 Updated efficacy data from a phase I trial in Hepatocellular carcinoma released by Blueprint
  • 18 Aug 2017 Updated efficacy and adverse events data from a phase I trial in Hepatocellular carcinoma released by Blueprint Medicines
  • 15 Dec 2016 Biomarkers information updated
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