Research programme: bone morphogenetic protein type-1 receptor antagonist - La Jolla Pharmaceutical/Vanderbilt University
Alternative Names: BMP type-I receptor antagonist - La Jolla Pharmaceutical/Vanderbilt UniversityLatest Information Update: 13 Mar 2025
At a glance
- Originator Vanderbilt University Medical Center
- Class Small molecules
- Mechanism of Action Bone morphogenetic protein receptor type I antagonists
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Fibrodysplasia ossificans progressiva; Musculoskeletal disorders