Research programme: glucosylceramide biobetter - Bionaturis
Alternative Names: BNT 001Latest Information Update: 22 Aug 2016
At a glance
- Originator Bionaturis
- Class Biobetters; Glucosidases
- Mechanism of Action Glucosylceramidase replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Gaucher's disease type I
Most Recent Events
- 22 Aug 2016 Discontinued for Gaucher's disease type I in Spain (PO)