Research programme: mRNA therapeutics - Arcturus Therapeutics/Ultragenyx Pharmaceutical

Drug Profile

Research programme: mRNA therapeutics - Arcturus Therapeutics/Ultragenyx Pharmaceutical

Alternative Names: LUNAR-GSDIII

Latest Information Update: 18 May 2018

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At a glance

  • Originator Arcturus Therapeutics
  • Developer Arcturus Therapeutics; Ultragenyx Pharmaceutical
  • Class RNA
  • Mechanism of Action RNA inhibitors; RNA interference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

  • New Molecular Entity Yes

Highest Development Phases

  • Preclinical Unspecified

Most Recent Events

  • 14 May 2018 Preclinical trials in Undefined indication in USA (Parenteral)
  • 16 Mar 2016 Arcturus Therapeutics receives intent to grant notice from the European Patent Office for their unlocked nucleomonomer agent (UNA) Technology
  • 29 Oct 2015 Early research in Undefined indication in USA (Parenteral)
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