Orphan disease gene therapy - GlaxoSmithKline
Alternative Names: Rare disease therapeutics - GSKLatest Information Update: 27 Dec 2019
At a glance
- Originator GlaxoSmithKline
- Developer GlaxoSmithKline; Oxford BioMedica
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Unspecified